Table 1

Autosomal dominant neurodegenerative diseases [97-98]

Disease
Mutant Gene
Mutation
Transgenic Mouse Model

FAD
APP
Mainly missense
Mutant APP and APP:PS1
FAD
PS1
Mainly missense
Mutant PS1
FAD
PS2
Mainly missense
Mutant PS2
FALS
SOD1
Mainly missense
Mutant SOD1
FTDP-17
Tau
Missense & splice
Mutant Tau
PD
α-synuclein
Missense
wt/mutant αsyn
Prion
PrP
Mainly missense
Mutant PrP
HD
huntingtin
Polyglutamine
huntingtin (expanded repeat)
SCA-1
ataxin-1
Polyglutamine
ataxin-1 (expanded repeat)
SCA-3
ataxin-3
Polyglutamine
ataxin-3 (expanded repeat)
DRPLA
atrophin-1
Polyglutamine
atrophin-1 (expanded repeat)

FAD: Familial Alzheimer's Disease FALS: Familial amyotrophic lateral sclerosis with Parkinsonism HD: Huntington's Disease DRPLA: Dentatorubral and pallidoluysian atrophy PD: Parkinson's Disease SCA: Spinocerebellar ataxias FTDP: Frontotemporal Dementia

Chan Reproductive Biology and Endocrinology 2004 2:39   doi:10.1186/1477-7827-2-39